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mmcc53
10-06-2006, 11:40 AM
Data Presented at Academy of Managed Care Pharmacy's Educational

Conference Also Highlight Impact of TYSABRI(R) on Quality of Life and

Cost Effectiveness of MS Therapies



Biogen Idec (NASDAQ: BIIB) and Elan Corporation, plc (NYSE: ELN) announced that

data to be presented today at the Academy of Managed Care Pharmacy's (AMCP) 2006

Educational Conference in Chicago, IL show that in Phase III studies TYSABRI(R)

(natalizumab) therapy significantly reduced corticosteroid use and

hospitalizations, and increased the proportion of MS patients with no disease

activity. Findings will also be presented that demonstrate the positive impact

of TYSABRI on a number of health-related quality of life of measures (QoL) and

the cost-effectiveness of MS therapies.



Data Demonstrate TYSABRI Reduced Corticosteroid Use, Hospitalizations and

Increases the Proportion of Disease-Free Patients



Data presented today from the AFFIRM monotherapy study (two-year, randomized,

multi-center, placebo-controlled, double-blind study of 942 patients conducted

in 99 sites worldwide), showed the impact of TYSABRI on two pre-specified

endpoints, the annualized rate of relapses requiring corticosteroid use and the

annualized rate of hospitalizations due to MS. Data showed there was a 69%

relative reduction in the annualized rate of relapses requiring steroids for

patients treated with TYSABRI compared to those treated with placebo (0.133 in

the TYSABRI group vs. 0.432 in the placebo group(p<0.001)). The study also

showed that TYSABRI therapy resulted in a 65% relative reduction in the

annualized rate of MS-related hospitalizations over two years (0.034 in the

TYSABRI group vs. 0.097 in the placebo group(p<0.001)).



A post-hoc analysis was also conducted to determine the proportion of patients

free of disease activity over two years. To determine this, a retrospective

analysis was conducted to evaluate both clinical and magnetic resonance imaging

(MRI) measures. Patients with no disease activity were defined as patients who

experienced no additional relapses or progression of physical disability and

exhibited stable MRI measures without any new gadolinium-enhancing,

T2-hyperintense, or T1-hypointense lesions. Data presented today suggest that

TYSABRI significantly increased the proportion of disease-free patients by 79%

over two years compared with placebo (28% vs. 6%, respectively; p<0.001).



Cost Effectiveness of MS Therapies



A model was constructed by Xcenda, formerly Applied Health Outcomes, to compare

the cost per relapse avoided among the five approved disease-modifying MS

therapies to treat relapsing forms of MS. Overall cost of therapy was calculated

using the US ********* acquisition drug cost, and costs associated with drug

administration, patient monitoring and treatment of relapses. The costs

associated with adverse events were not assessed as part of this model.

Effectiveness was defined as the number of relapses avoided with treatment,

which was calculated as the number of relapses for a non-treated population

multiplied by published relapse rate reductions for the therapies.(1) Based on

the model developed, the cost per relapse per year avoided was lowest for

TYSABRI. The cost per relapse avoided for TYSABRI was between $12,730 and

$23,274 lower than that of the other approved disease-modifying therapies.



Data Show TYSABRI Had Improvement in Quality of Life Assessments



Quality of Life (QoL) was assessed using three different measures, the Multiple

Sclerosis Quality of Life Inventory (MSQLI), the Short Form-36 Health Survey

(SF-36), which is a component of the MSQLI, and a Visual Analogue Scale (VAS).

The MSQLI is an MS-specific battery of 10 scales that measure disease impact on

QoL, including fatigue, pain, sexual function, bowel and bladder function,

visual impairment, mental health and need for social support. The SF-36 is

comprised of 36 questions designed to assess patients' physical and mental

well-being. General well-being was also measured using the VAS. In data

presented today from the AFFIRM study, patients in the TYSABRI-treated group

realized a significant improvement in physical measures of the SF-36 compared

with a decline in the placebo-treated group (p=0.003). A significant improvement

was also seen in the mental component of the SF-36 in patients treated with

TYSABRI compared with a decline in the placebo-group (p=0.011). Significant

benefits were also seen using the VAS (p=0.007). About TYSABRI



In the US, TYSABRI is approved as a monotherapy treatment for relapsing forms of

MS. TYSABRI increases the risk of progressive multifocal leukoencephalopathy

(PML), an opportunistic viral infection of the brain that usually leads to death

or severe disability. Patients should be monitored at regular intervals for any

new or worsening signs or symptoms suggestive of PML. Because of the increased

risk of PML, TYSABRI is generally recommended for patients who have had an

inadequate response to, or are unable to tolerate, alternate MS therapies. It is

available in the US only through a restricted distribution program called the

TOUCH Prescribing Program. According to product labeling, after two years,

TYSABRI treatment led to a 67% relative reduction (p<0.001) in the annualized

relapse rate compared to placebo and reduced the relative risk of disability

progression by 42% (p<0.001). TYSABRI treatment also resulted in sustained and

statistically significant reductions in brain lesion activity as measured by

MRI. Changes in MRI findings often do not correlate with changes in the clinical

status of patients (e.g., disability progression). The prognostic significance

of the MRI findings in these studies has not been evaluated.



In the European Union, TYSABRI is indicated as a single disease-modifying

therapy in highly active relapsing-remitting MS patients. Because of the

increased risk of PML, it is for patients with high disease activity despite

treatment with a beta-interferon or in patients with rapidly evolving severe

relapsing-remitting MS. According to product labeling in the EU, after two

years, TYSABRI treatment led to a 68% relative reduction (p<0.001) in the

annualized relapse rate compared to placebo and reduced the relative risk of

disability progression by 42-54% (p<0.001).



Serious adverse events that occurred in TYSABRI-treated patients included

hypersensitivity reactions (e.g., anaphylaxis), infections, depression and

gallstones. In MS trials, the incidence and rate of other serious and common

adverse events, including the overall incidence and rate of infections, were

balanced between treatment groups. Herpes infections were slightly more common

in patients treated with TYSABRI. Serious opportunistic and other atypical

infections have been observed in TYSABRI-treated patients, some of whom were

receiving concurrent immunosuppressants. Common adverse events reported in

TYSABRI-treated patients include headache, fatigue, infusion reactions, urinary

tract infections, joint and limb pain, lower respiratory infections, rash,

gastroenteritis, abdominal discomfort, vaginitis, and diarrhea.



For more information about TYSABRI please visit www.tysabri.com,

www.biogenidec.com or www.elan.com, or call 1-800-456-2255.

*Joy*
10-06-2006, 12:58 PM
Thanks for the post, mmcc